Condition: Type 1 Diabetes (T1D)
Interventions: Drug: L. johnsonii Probiotic; Drug: Placebo Capsule
Sponsors: University of Florida; National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
Not yet recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days
Condition: Fetal Structural Anomalies
Intervention: Diagnostic Test: Prenatal Genomic Sequencing
Sponsors: Columbia University; Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Baylor College of Medicine; University of North Carolina; The George Washington University Biostatistics Center; Oregon Health and Science University
Recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days
Condition: Dementia
Interventions: Drug: 11C-ER176; Drug: 11C-PIB
Sponsor: National Institute of Mental Health (NIMH)
Not yet recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days
Condition: Spinal Muscular Atrophy
Intervention: Genetic: AVXS-101
Sponsors: United BioSource Corporation; AveXis, Inc.
Available
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days
Conditions: Focal Epilepsy; Intractable Epilepsy; Epileptic Encephalopathy; Lennox Gastaut Syndrome; Symptomatic Epilepsy; Generalized Epilepsy
Intervention: Device: Reveal LINQ ICM System
Sponsors: Northwell Health; Medtronic
Recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days
Condition: Sickle Cell Disease
Intervention: Device: HemeChip
Sponsors: University Hospitals Cleveland Medical Center; US federal government; Amino Kano Teaching Hospital; Murtala Mohammed Specialist Hospital; Hasiya Bayero Pediatric Hospital; University of Nebraska; University of North Carolina, Chapel Hill; Case Western Reserve University
Recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days
Condition: Infertility
Intervention: Genetic: double strand break
Sponsor: Reproductive Medicine Associates of New Jersey
Recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days
Condition: MELAS Syndrome
Intervention: Drug: L-Citrulline
Sponsors: Baylor College of Medicine; National Institutes of Health (NIH); University of South Florida; Columbia University
Not yet recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days
Conditions: Lysosomal Diseases; Gangliosidosis; GM1
Intervention: Biological: AAV9-GLB1
Sponsor: National Human Genome Research Institute (NHGRI)
Recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days
Condition: Wolfram Syndrome
Intervention:
Sponsor: Washington University School of Medicine
Recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days





