Condition: Spinal Muscular Atrophy
Intervention: Genetic: AVXS-101
Sponsors: United BioSource Corporation; AveXis, Inc.
Available
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days
AveXis Managed Access Program Cohort for Access to AVXS-101
May 21, 2019ClinicalTrials.govComments OffGenetic DiseaseAccess | AveXis | AVXS101 | Cohort | Managed | Program
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