Genetic Disease

Linking Epigenomics With Prescription Opioid Abuse and High Impact Musculoskeletal Pain

Conditions:   Pain, Chronic;   Prescription Drug Abuse (Not Dependent)
Intervention:  
Sponsor:   University of Florida
Not yet recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days

May 13, 2019Comments OffAbuse | Epigenomics | High | Impact | Linking | Musculoskeletal | Opioid | Pain | Prescription
Extension Study to Evaluate the Long-Term Effects of ACE-083 in Patients With Facioscapulohumeral Muscular Dystrophy (FSHD) and Charcot-Marie Tooth (CMT) Disease Types 1 and X (CMT1 and CMTX)

Conditions:   Facioscapulohumeral Muscular Dystrophy;   Charcot-Marie-Tooth Disease
Intervention:   Drug: ACE-083
Sponsor:   Acceleron Pharma, Inc.
Recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days

May 12, 2019Comments OffACE083 | CharcotMarie | CMT1 | CMTX | Disease | Dystrophy | Effects | Evaluate | Extension | Facioscapulohumeral | FSHD | Longterm | Muscular | Patients | Study | Tooth | Types
Genetics and Shared Decision Making in Improving Care for Patients With Stage IVA-C Non-small Cell Lung Cancer

Conditions:   Activating ALK Gene Mutation Negative;   Activating EGFR Gene Mutation Negative;   Activating ROS1 Gene Mutation Negative;   Health Care Provider;   Lung Non-Small Cell Carcinoma;   Stage IV Lung Cancer AJCC v8;   Stage IVA Lung Cancer AJCC v8;   Stage IVB Lung Cancer AJCC v8
Interventions:   Other: Counseling;   Other: Questionnaire Administration;   Other: Medical Chart Review
Sponsor:   Thomas Jefferson University
Recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days

May 11, 2019Comments OffCancer | Care | Cell | Decision | Genetics | Improving | IVAC | Lung | Making | NonSmall | Patients | Shared | Stage
A Phase I Study of Niraparib Administered Concurrently With Postoperative RT in Patients With Triple Negative Breast Cancer and an Incomplete Pathologic Response

Conditions:   Triple Negative Breast Cancer;   Residual Disease
Interventions:   Drug: Niraparib;   Radiation: Radiation Therapy
Sponsors:   Massachusetts General Hospital;   Tesaro, Inc.
Not yet recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days

May 10, 2019Comments OffAdministered | Breast | Cancer | Concurrently | Incomplete | Negative | Niraparib | Pathologic | Patients | Phase | Postoperative | Response | Study | Triple
Ibrutinib and Venetoclax in Treating Patients With Chronic Lymphocytic Leukemia After Ibrutinib Resistance

Conditions:   Chronic Lymphocytic Leukemia;   Loss of Chromosome 17p
Interventions:   Drug: Ibrutinib;   Drug: Venetoclax
Sponsors:   Kerry Rogers;   National Cancer Institute (NCI);   Janssen Research & Development, LLC
Not yet recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days

May 9, 2019Comments OffAfter | Chronic | Ibrutinib | Leukemia | Lymphocytic | Patients | Resistance | Treating | Venetoclax
Collection of Human Biospecimens for Basic and Clinical Research Into Alpha Globin Variants

Conditions:   Alpha Thalassemia;   Sickle Cell Disease;   Malaria;   Human Physiology
Intervention:  
Sponsor:   National Institute of Allergy and Infectious Diseases (NIAID)
Recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days

May 8, 2019Comments OffAlpha | Basic | Biospecimens | Clinical | Collection | Globin | Human | Into | Research | Variants
Peer i-Coaching for Activated Self-Management Optimization in Adolescents and Young Adults With Chronic Conditions

Conditions:   Sickle Cell Disease;   Chronic Kidney Diseases;   Systemic Lupus Erythematosus;   Childhood Cancer;   Inflammatory Bowel Diseases;   Asthma;   Stem Cell Transplant;   Organ Transplant;   Diabetes Mellitus, Type 1
Interventions:   Behavioral: PiCASO Intervention Group;   Behavioral: Sham Comparator: Attention Control Group
Sponsors:   Duke University;   National Institutes of Health (NIH);   National Institute of Nursing Research (NINR)
Not yet recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days

May 7, 2019Comments OffActivated | Adolescents | Adults | Chronic | Conditions | iCoaching | Optimization | Peer | SelfManagement | Young
Adoptive Transfer of Tumor Infiltrating Lymphocytes for Advanced Solid Cancers

Conditions:   Gastric Cancer;   Colorectal Cancer;   Pancreatic Cancer;   Sarcoma;   Mesothelioma;   Neuroendocrine Tumors;   Squamous Cell Cancer;   Merkel Cell Carcinoma;   Mismatch Repair Deficiency;   Microsatellite Instability
Interventions:   Biological: Tumor Infiltrating Lymphocytes (TIL);   Drug: Fludarabine + Cyclophosphamide combination
Sponsor:   Udai Kammula
Not yet recruiting
ClinicalTrials.gov: Genetic_Disease | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days

May 4, 2019Comments OffAdoptive | Advanced | Cancers | Infiltrating | Lymphocytes | Solid | Transfer | Tumor