Intravenous Gene Transfer With an AAV9 Vector Expressing Human

Conditions:   Lysosomal Diseases;   Gangliosidosis;   GM1
Intervention:   Biological: AAV9-GLB1
Sponsor:   National Human Genome Research Institute (NHGRI)
Recruiting
ClinicalTrials.gov: Neurology | Recruiting, Not yet recruiting, Available Studies | United States | First posted in the last 100 days